uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 5, 2020
RegMed Investors’ (RMi) closing bell: sold-out by strength
June 4, 2020
RegMed Investors’ (RMi) closing bell: sector set-back
June 3, 2020
RegMed Investors’ (RMi) closing bell: cause and effect
June 3, 2020
RegMed Investors’ (RMi) pre-open: tear gas drifts over optimism on the curfewed and reopening streets
June 2, 2020
RegMed Investors’ (RMi) closing bell: are “things” good or less bad
June 1, 2020
RegMed Investors’ (RMi) closing bell: rowdy times starts a new month
May 30, 2020
RegMed/Cell and Gene Therapy Earnings Scorecard - Q1/20 - to date
May 29, 2020
RegMed Investors’ (RMi) closing bell: ricochet, trading drags and pops on last session of month
May 28, 2020
RegMed Investors’ (RMi) closing bell: a rally until it wasn’t, the sector’s surge got erased
May 28, 2020
RegMed Investors’ (RMi) pre-open: dicey
35 companies, 1 interpreter!
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