uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 6, 2020
RegMed Investors’ (RMi) closing bell: trade what you see, the highs
July 2, 2020
RegMed Investors’ (RMi) closing bell: less bad
July 1, 2020
RegMed Investors’ (RMi) closing bell: sector racks it up
June 30, 2020
RegMed Investors’ (RMi) closing bell: last trading day of month rallies solidifying the quarter
June 30, 2020
RegMed Investors’ (RMi) pre-open: the roller-coaster keeps rolling
June 29, 2020
RegMed Investors’ (RMi) closing bell: sector open positive, slowly weakening as the session closed
June 29, 2020
RegMed Investors’ (RMi) pre-open: after a dive, there’s sometimes a jive
June 26, 2020
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector got sacked
June 26, 2020
RegMed Investors’ (RMi) pre-open: stress tests, bad infection news, weakness is driving sentiment’s direction
June 25, 2020
RegMed Investors’ (RMi) closing bell: surge, purge and gorge
35 companies, 1 interpreter!
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