uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
February 18, 2020
RegMed Investors’ (RMi) pre-open: low volume had constipated share pricing
February 17, 2020
RegMed Investors’ (RMi) closing bell: markets are closed for President's Day holiday
February 12, 2020
RegMed Investors’ (RMi) closing bell: same theme, different session
February 11, 2020
RegMed Investors’ (RMi) closing bell: fear of coronavirus or a beer in this market climate?
February 10, 2020
RegMed Investors’ (RMi) closing bell: optimism returns as electronic trading grinds the oversold sector higher as the coronavirus panic wanes
February 7, 2020
RegMed Investors’ (RMi) closing bell: another falling session
February 6, 2020
RegMed Investors’ (RMi) closing bell: don’t chase short-term momentum
February 5, 2020
RegMed Investors’ (RMi) closing bell: expectation, a strong belief that something will happen or be the case in the future
February 3, 2020
RegMed Investors’ (RMi) closing bell: the return of the oversold from the coronavirus influence
January 31, 2020
RegMed Investors’ (RMi) closing bell: cavernous cell and gene therapy sector trends
35 companies, 1 interpreter!
Insight, foresight and recommendation
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