uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 30, 2020
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector oozes to another pool of blood
January 29, 2020
RegMed Investors’ (RMi) closing bell: careful as the sector trends
January 28, 2020
RegMed Investors’ (RMi) closing bell: we are not through with scaling the wall of worry
January 27, 2020
RegMed Investors’ (RMi) pre-open: uncertainty continues to weigh on market sentiment leaving most unnerved
January 25, 2020
RegMed Investors' (RMi) closing bell: which risks are playing-out that haven't already been there?
January 24, 2020
RegMed Investors’ (RMi) pre-open: cell and gene therapy sanity is at stake
January 23, 2020
RegMed Investors’ (RMi) closing bell: a negative close, after a positive following a negative close and a holiday
January 23, 2020
RegMed Investors’ (RMi) pre-open: who’s on first, what’s on second?
January 22, 2020
RegMed Investors’ (RMi) closing bell: the sector grinds and creeps higher
January 22, 2020
RegMed Investors’ (RMi) pre-open: the oversold shall rise again
35 companies, 1 interpreter!
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