uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 27, 2019
RegMed Investors’ (RMi) closing bell: another slippery slope and sliding sector as risk defines the investment pattern
December 26, 2019
RegMed Investors’ (RMi) closing bell: the sector tripped after all the good cheer
December 24, 2019
RegMed Investors’ (RMi) closing bell: a complacent session for indexes
December 24, 2019
RegMed Investors’ (RMi) pre-open: a shortened session
December 23, 2019
RegMed Investors’ (RMi) closing bell: the upside needle moved after a quadruple witching Friday and collaboration transactions
December 20, 2019
RegMed Investors’ (RMi) closing bell:the sector closed down after Thursday’s spurt
December 20, 2019
RegMed Investors’ (RMi) pre-open: TGIF
December 19, 2019
RegMed Investors’ (RMi) closing bell: the sector jumped after two down sessions
December 18, 2019
RegMed Investors’ (RMi) closing bell: the sector is counterintuitive as today’s NASDAQ index inclined as my covered composite of companies declined
December 17, 2019
RegMed Investors’ (RMi) closing bell: sector breaks down as profiteering circles the upside
35 companies, 1 interpreter!
Insight, foresight and recommendation
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