uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 21, 2020
RegMed Investors’ (RMi) closing bell: the cell and gene therapy dived
January 17, 2020
RegMed Investors’ (RMi) closing bell: the sector slips and slides
January 16, 2020
RegMed Investors’ (RMi) closing bell: stability hangs in the balance, 7 positive out of 12 closes have kept the cell and gene therapy sector flinching
January 15, 2020
RegMed Investors’ (RMi) closing bell: am I going deaf?
January 13, 2020
RegMed Investors’ (RMi) closing bell: day one (1) of JPMorgan and a share pricing downer
January 11, 2020
RegMed Investors’ (RMi) closing bell: as I wrote, the downside slide is starting
January 9, 2020
RegMed Investors’ (RMi) closing bell: many share pricing and valuations are tipping the scales
January 8, 2020
RegMed Investors’ (RMi) closing bell: the sector’s rise defused by lightening of political rhetoric
January 3, 2020
RegMed Investors’ (RMi) closing bell: volatility sets the tone for first two trading sessions post a holiday
January 2, 2020
RegMed Investors’ (RMi) closing bell: starting the year with another downside rotation from Tuesday’s close
35 companies, 1 interpreter!
Insight, foresight and recommendation
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