uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 24, 2019
RegMed Investors’ (RMi) closing bell: Low volume and percentage moves do not glamorize the sector for short-term investment
October 23, 2019
RegMed Investors’ (RMi) closing bell: the ceiling hasn’t fallen yet, the leaks are increasing
October 18, 2019
RegMed Investors’ (RMi) closing bell: escaping the maze of the oversold
October 17, 2019
RegMed Investors’ (RMi) closing bell: three (3) up sessions and counting
October 16, 2019
RegMed Investors’ (RMi) closing bell: low volume and minimal percentage moves
October 15, 2019
RegMed Investors’ (RMi) closing bell: the oversold were on the road to a comeback
October 9, 2019
RegMed Investors’ (RMi) closing bell: it wasn’t the outcome I had expected i.e. sector weakness
October 5, 2019
RegMed Investors’ (RMi) closing bell: a “goldilocks” upside move
October 3, 2019
RegMed Investors’ (RMi) closing bell: after weakness, there’s neutrality – like today and it is sure to spiral again
October 2, 2019
RegMed Investors’ (RMi) closing bell: where the sector meets the road too long traveled
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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