uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 4, 2019
RegMed Investors’ (RMi) closing bell: the market rips, the sector dips on the second session of November
October 31, 2019
RegMed Investors’ (RMi) closing bell: The sector risks are still to the downside
October 28, 2019
RegMed Investors’ (RMi) closing bell: indexes set new records
October 26, 2019
RegMed Investors’ (RMi) closing bell: the oversold are flirting with the upside and it ain’t a love match
October 25, 2019
RegMed Investors’ (RMi) pre-open: the read-out of the coming open – subdued
October 24, 2019
RegMed Investors’ (RMi) closing bell: Low volume and percentage moves do not glamorize the sector for short-term investment
October 23, 2019
RegMed Investors’ (RMi) closing bell: the ceiling hasn’t fallen yet, the leaks are increasing
October 18, 2019
RegMed Investors’ (RMi) closing bell: escaping the maze of the oversold
October 17, 2019
RegMed Investors’ (RMi) closing bell: three (3) up sessions and counting
October 16, 2019
RegMed Investors’ (RMi) closing bell: low volume and minimal percentage moves
35 companies, 1 interpreter!
Insight, foresight and recommendation
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