uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 1, 2019
RegMed Investors’ (RMi) closing bell: falling victim to sentiment
October 1, 2019
RegMed Investors’ (RMi) pre-open: new month and quarter
September 30, 2019
RegMed Investors’ (RMi) closing bell: it’s been a rough ride
September 29, 2019
RegMed Investors’ (RMi) closing bell: another session of sorrow
September 26, 2019
RegMed Investors’ (RMi) closing bell: the roller-coaster rolls down
September 18, 2019
RegMed Investors’ (RMi) closing bell: trounced again
September 17, 2019
Clone of RegMed Investors’ (RMi) closing bell: the sector turns and burns
September 17, 2019
RegMed Investors’ (RMi) closing bell: the sector turns and burns
September 16, 2019
RegMed Investors’ (RMi) closing bell: yippie-yi-yo-kai-yay
September 13, 2019
RegMed Investors’ (RMi) closing bell: equities fell, not as far but, still down
35 companies, 1 interpreter!
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