uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 27, 2019
RegMed Investors’ (RMi) pre-open: want to play on the sector seesaw?
August 26, 2019
RegMed Investors’ (RMi) closing bell: the sector in relation to this market, optimism, hesitancy or fatalism, I’m split
August 25, 2019
RegMed Investors’ (RMi) Friday’s closing bell: another sector goose egg of a session
August 22, 2019
RegMed Investors’ (RMi) closing bell: short-term fear has battered the cell and gene therapy sector
August 22, 2019
RegMed Investors’ (RMi) pre-open: musical chairs, look to the left and then right
August 21, 2019
RegMed Investors’ (RMi) closing bell: another high after a dive
August 20, 2019
RegMed Investors’ (RMi) closing bell: the sector dike sprung a leak and equities poured-out
August 20, 2019
RegMed Investors’ (RMi) pre-open: skim if you can trim, buy if it will fly and sell if compelled!
August 19, 2019
RegMed Investors’ (RMi) closing bell: the sector rallied
August 13, 2019
RegMed Investors’ (RMi) closing bell: the sector flipped up but, didn’t soar
35 companies, 1 interpreter!
Insight, foresight and recommendation
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