uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 9, 2019
RegMed Investors’ (RMi) closing bell: no real movement from the open
September 8, 2019
RegMed Investors’ (RMi) closing bell: back to a softening sector as the NASDAQ dips
September 6, 2019
RegMed Investors’ (RMi) pre-open: up, up and are we totally away
September 5, 2019
RegMed Investors’ (RMi) closing bell: trade and economic news drives the market higher
September 5, 2019
RegMed Investors’ (RMi) closing bell: from a negative open to a positive close
September 3, 2019
RegMed Investors’ (RMi) closing bell: Cell and gene therapy equities fell, the first trading day of a historically tough month
August 30, 2019
RegMed Investors’ (RMi) closing bell: the week and August – they’re over
August 29, 2019
RegMed Investors’ (RMi) closing bell: surging sector but, expect the rush upside to subside
August 28, 2019
RegMed Investors’ (RMi) closing bell: as we move through the market’s grounds
August 27, 2019
RegMed Investors’ (RMi) closing bell: when one side of the seesaw empties, the other drops like a stone
35 companies, 1 interpreter!
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