uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 24, 2016
RegMed’s close: Friday ends the week not as a wall but, more like a door
April 22, 2016
Lower open expected; RegMed sector, expectations for the short-term influence our universe
April 21, 2016
RegMed’s close: the truck I mentioned in the pre-open left fully loaded
April 14, 2016
RegMed’s close: small gains except XON and larger losses on moderate volume
April 13, 2016
RegMed’s close: trading momentum moved the iShares Nasdaq Biotechnology ETF (IBB) +1.91% higher
April 11, 2016
RegMed’s close: a good start and then the sector fades …
April 8, 2016
RegMed’s close: the intensity of the bounce likens to rodeo riding
April 7, 2016
RegMed’s close: everything works then, nothing stays
April 6, 2016
RegMed’s close: yesterday’s oversold positions tipped value’s scale
April 5, 2016
RegMed’s close: the sector finds value by selling …
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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