uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 25, 2015
RegMed’s close: the sector that was stretchered to new lows
September 25, 2015
Higher open expected; RegMed, the optimism among investors is mainly due to Yellen’s speech, while the sector is swimming upstream against a strong current
September 24, 2015
RegMed’s close: yesterday was a bad day and today was a bit better
September 24, 2015
Lower open expected; RegMed’s decliners are decreasing but, it is time to dig for those with upside potential
September 22, 2015
RegMed's close: a sector with its tail between its legs, feed the dog and he will wag
September 22, 2015
Lower open expected; RegMed put an ear on the rail to figure out what’s going on!
September 21, 2015
RegMed’s close: sector skipped like a stone thrown and sank deep in the red; my pre-open pattern spoke – it wasn’t just about Hillary!
September 21, 2015
uniQure (QURE)announced the topline results of one-year follow-up data from a P1/2 clinical trial - HOLD
September 21, 2015
Higher open expected; RegMed has five up days, the “pattern” worries me?
September 18, 2015
RegMed’s close: sector’s variability due to vulnerability of sentiment combined with quadruple witching
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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