uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
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December 23, 2024
RegMed Investors (RMi) Closing Bell: A merry and happy holiday-short week
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RegMed Investors (RMi) Closing Bell: all cell and gene therapy sector stocks snap to attention
December 19, 2024
RegMed Investors (RMi) Closing Bell: econs are shoving the cell and gene therapy sector
December 18, 2024
RegMed Investors (RMi) Closing Bell: Jerome speaks with 25 basis point reduction and tanks the markets
December 17, 2024
RegMed Investors (RMi) Closing Bell: from the bottom of the stats, hits and balls keep sector on the board
December 16, 2024
RegMed Investors (RMi) Closing Bell: pop goes the sector
December 13, 2024
RegMed Investors (RMi) Closing Bell: bang, bang; struck in a trading range
December 13, 2024
RegMed Investors’ (RMi) pre-open: blood awash in the cell and gene therapy sector
December 12, 2024
RegMed Investors (RMi) Closing Bell: the haunting of share pricing continues
35 companies, 1 interpreter!
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