uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 23, 2024
RegMed Investors’ (RMi) pre-open: look for some cheaps and oversold
October 22, 2024
RegMed Investors (RMi) Closing Bell: forget sentiment
October 21, 2024
RegMed Investors (RMi) Closing Bell: slam, bam; the sectors in the can
October 16, 2024
RegMed Investors (RMi) Closing Bell: sector rises like the moon
October 15, 2024
RegMed Investors (RMi) Closing Bell: uncertainty and hesitation
October 14, 2024
RegMed Investors (RMi) Closing Bell: a follow through session from the trough after October’s start
October 11, 2024
RegMed Investors (RMi) Closing Bell: cell and gene therapy sector ascends, finally
October 10, 2024
RegMed Investors (RMi) Closing Bell: domino sector falling effect’s chain reaction
October 9, 2024
RegMed Investors (RMi) Closing Bell: the domino affect
October 8, 2024
RegMed Investors (RMi) Closing Bell: sector slightly spikes
35 companies, 1 interpreter!
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