uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 7, 2024
RegMed Investors (RMi) Closing Bell: no joy
October 4, 2024
RegMed Investors (RMi) Closing Bell: attention returned to the oversold cell and gene therapy sector
October 3, 2024
RegMed Investors (RMi) Closing Bell: this a.m.’s calling-out the downside, didn’t work
September 30, 2024
RegMed Investors (RMi) Closing Bell: ducking the shrapnel of exploding cell and gene therapy sector valuations
September 27, 2024
RegMed Investors (RMi) Closing Bell: the week that was as September and Q3 ends Monday
September 26, 2024
RegMed Investors (RMi) Closing Bell: sectors back in a positive close as econs follow expectation
September 25, 2024
RegMed Investors (RMi) Closing Bell: sector rumpled and tumbled
September 24, 2024
RegMed Investors (RMi) Closing Bell: Big disappointment, consumer confidence data
September 20, 2024
RegMed Investors (RMi) Closing Bell: triple witching Friday
September 19, 2024
RegMed Investors (RMi) Closing Bell: snap-crackle and a big pop
35 companies, 1 interpreter!
Insight, foresight and recommendation
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