uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 16, 2024
RegMed Investors (RMi) Closing Bell: rock-in the limbo dance
January 12, 2024
RegMed Investors (RMi) Closing Bell: a Friday’s opening jive followed by afternoon dive after 3-other weekly downfalls
January 9, 2024
RegMed Investors (RMi) Closing Bell: Volatility is high as selling/profit-taking amplified
December 27, 2023
RegMed Investors (RMi) Closing Bell: a Santa Claus rally in a short week of pitstops
December 26, 2023
RegMed Investors (RMi) Closing Bell: holiday cheer is still with us as cell and gene therapy sector continues to cascade
December 22, 2023
RegMed Investors (RMi) Closing Bell: Happy Hanukkah, Merry Christmas and Holiday; travel safe
December 20, 2023
RegMed Investors (RMi) Closing Bell: merry, merry-go-round
December 19, 2023
RegMed Investors (RMi) Closing Bell: volatility is its middle name even as news doesn’t help
December 18, 2023
RegMed Investors (RMi) Closing Bell: another downturn after a Friday downswing
December 15, 2023
RegMed Investors (RMi) Closing Bell: triple witching’ Friday
35 companies, 1 interpreter!
Insight, foresight and recommendation
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