uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
February 20, 2024
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February 16, 2024
RegMed Investors (RMi) Closing Bell: the cell and gene therapy closed barely positive after a bumpy session
February 15, 2024
RegMed Investors (RMi) Closing Bell: riding the bull
February 14, 2024
RegMed Investors (RMi) Closing Bell: yippee-kai-yay
February 9, 2024
RegMed Investors (RMi) Closing Bell: hang-on to reward prospects for a while
February 8, 2024
RegMed Investors (RMi) Closing Bell: share prices rides on the sector’s merry-go-round
February 7, 2024
RegMed Investors (RMi) Closing Bell: The RegMed sector was stuck with sentiment diarrhea
February 5, 2024
RegMed Investors (RMi) Closing Bell: cell and gene therapy sector passes more gas
February 1, 2024
RegMed Investors (RMi) Closing Bell: back on the roller-coaster
January 26, 2024
RegMed Investors (RMi) Closing Bell: strapped-in for a rough ride
35 companies, 1 interpreter!
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