uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 1, 2023
RegMed Investors’ (RMi) closing bell: waiting and wanting earnings LPS (loss-per-share) having started to be over
August 1, 2023
RegMed Investors’ (RMi) pre-open: stock futures lower as earnings’ releases begin
July 31, 2023
RegMed Investors’ (RMi) closing bell: July ends on high note while sector LPS (loss-per-share) earnings are about to start
July 27, 2023
RegMed Investors’ (RMi) closing bell: can share pricing slides be cured?
July 25, 2023
RegMed Investors’ (RMi) closing bell: softening outlook
July 12, 2023
RegMed Investors’ (RMi) closing bell: an upside theatre
July 11, 2023
RegMed Investors’ (RMi) closing bell: caution seems to be the sector’s word for the session
July 7, 2023
RegMed Investors’ (RMi) closing bell: old uncle algorithms came to visit
June 30, 2023
RegMed Investors’ (RMi) closing bell: the oxygen machine was turned back on so the sector could climb the wall of worry
June 28, 2023
RegMed Investors’ (RMi) closing bell: it ain’t over, sentiment is testing resistance
35 companies, 1 interpreter!
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