uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 8, 2022
RegMed Investors’ (RMi) pre-open: vote your conscious and your portfolio
November 7, 2022
RegMed Investors’ (RMi) closing bell: election and economics will determine the week as negative momentum moves the sector today
November 4, 2022
RegMed Investors’ (RMi) closing bell: strolling a crooked session (10 of 35 covered companies stumbled)
November 4, 2022
RegMed Investors’ (RMi) pre-open: We need to understand the macro to comprehend the micro re “our” universe of cell and gene therapy companies
November 3, 2022
RegMed Investors’ (RMi) closing bell: taking it in the shins as sector trips
November 3, 2022
RegMed Investors’ (RMi) pre-open: gains followed by pain; so, what’s on-tap - earnings
November 2, 2022
RegMed Investors’ (RMi) closing bell: We waited for Jerome and got the expected .75 basis point rate increase
October 31, 2022
RegMed Investors’ (RMi) closing bell: falling and feeling more than a pinch as October ends
October 27, 2022
RegMed Investors’ (RMi) closing bell: I told you the downdraft was coming
October 26, 2022
RegMed Investors’ (RMi) closing bell: sector slips and slides, yet with positive close
35 companies, 1 interpreter!
Insight, foresight and recommendation
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