uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 26, 2022
RegMed Investors’ (RMi) pre-open: electronic trading and algorithmic rules keep sentiment on a leash
October 24, 2022
RegMed Investors’ (RMi) closing bell: sector rains on last week’s parade
October 21, 2022
RegMed Investors’ (RMi) closing bell: no ladders needed; the tide went out and today came back in
October 20, 2022
RegMed Investors’ (RMi) closing bell: The upside didn’t last long after Wednesday’s extreme downside from an upside open
October 17, 2022
RegMed Investors’ (RMi) closing bell: support levels are back for the oversold, although with low volume
October 14, 2022
RegMed Investors’ (RMi) closing bell: risk and sentiment have broken through cell and gene therapy equities
October 14, 2022
RegMed Investors’ (RMi) pre-open: an absence of certainty in inflation and earnings
October 12, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector share pricing rides the roller-coaster
October 11, 2022
RegMed Investors’ (RMi) closing bell: an oversold bounce from nowhere to close neutral in my coverage group
35 companies, 1 interpreter!
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