uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 18, 2022
RegMed Investors’ (RMi) closing bell: this week the cell and gene therapy sector equities got “whacked’ on the knuckles, today it got a pat on the back!
November 17, 2022
RegMed Investors’ (RMi) closing bell: skipping stones and stocks
November 16, 2022
RegMed Investors’ (RMi) closing bell: tampering and dampening share price
November 16, 2022
RegMed Investors’ (RMi) pre-open: whatever floats your boat or fills your portfolio, short-term moves could defend your positions
November 11, 2022
RegMed Investors’ (RMi) closing bell: closing out the week booking gains
November 10, 2022
RegMed Investors’ (RMi) closing bell: the risk-on fervor sent markets skyward and sector upward
November 10, 2022
RegMed Investors’ (RMi) pre-open: CPI, up +0.4% versus +0.6% estimate
November 9, 2022
RegMed Investors’ (RMi) closing bell: down sliding markets and sector responds to incomplete election results
November 9, 2022
RegMed Investors’ (RMi) pre-open: stock futures trade lower as election results are tallied
November 8, 2022
RegMed Investors’ (RMi) closing bell: after five (5) down sessions, it was inevitable that the algorithms would “rule”
35 companies, 1 interpreter!
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