uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 31, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector coverage ends August on a neutral note
August 30, 2022
RegMed Investors’ (RMi) closing bell: approaching August’s end with more sector declines
August 29, 2022
RegMed Investors’ (RMi) closing bell: a wobbly start on Monday post Friday’s sell-off
August 29, 2022
RegMed Investors’ (RMi) pre-open: Ripping-off shareholders as share pricing declines, inclines and degenerates
August 25, 2022
RegMed Investors’ (RMi) closing bell: why is the sector alternating between momentum driven upside and downside?
August 24, 2022
RegMed Investors’ (RMi) closing bell: The “merry-go-round” effect
August 22, 2022
RegMed Investors’ (RMi) closing bell: Volatility and resistance rule, five (5) sessions in a row
August 19, 2022
RegMed Investors’ (RMi) closing bell: feeling the low while experiencing “positioning complexity”
August 19, 2022
RegMed Investors’ (RMi) pre-open: the cell and gene therapy sector begs for direction on option expiration Friday
August 18, 2022
RegMed Investors’ (RMi) closing bell: slipping, sliding and with some upside gliding before the close
35 companies, 1 interpreter!
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