uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 14, 2022
RegMed Investors’ (RMi) pre-open: after a fall on Tuesday’, there’s still blood on the street as Producer Price Index (PPI) is down -0.1%
September 13, 2022
RegMed Investors’ (RMi) closing bell: no chicken dinner as sector and indexes got kicked to the floor while inflation numbers become an unequivocal negative for equities
September 13, 2022
RegMed Investors’ (RMi) pre-open: watch and wait to make a buck
September 9, 2022
RegMed Investors’ (RMi) closing bell: the share pricing levy is leaking from the morning’s opening
September 9, 2022
RegMed Investors’ (RMi) pre-open: share pricing runs
September 8, 2022
RegMed Investors’ (RMi) pre-open: yesterday’s added value was a gift
September 7, 2022
RegMed Investors’ (RMi) closing bell: A reaction to the market while electronic trading and algorithms recoup their sell “rules”
September 7, 2022
RegMed Investors’ (RMi) pre-open: the issues; resistance, the lack of support, conviction and relative strength
September 6, 2022
RegMed Investors’ (RMi) closing bell: sector takes it in the shins as value propositions get lost in sentiment’s retreat
35 companies, 1 interpreter!
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