uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 28, 2020
RegMed Investors’ (RMi) closing bell: sector seesaws to a neutral close
September 25, 2020
RegMed Investors’ (RMi) closing bell: what a difference volatility makes after yesterday’s 3 incliners versus today’s 32 incliners of 35 covered
September 25, 2020
RegMed Investors’ (RMi) pre-open: ain’t feelin’ the love
September 24, 2020
RegMed Investors’ (RMi) closing bell: sector gets snookered again
September 23, 2020
RegMed Investors’ (RMi) closing bell: many are called out but, few feel the upside
September 22, 2020
RegMed Investors’ (RMi) closing bell: what a distance an afternoon moves
September 21, 2020
RegMed Investors’ (RMi) closing bell: uncertainty impales the sector
September 21, 2020
RegMed Investors’ (RMi) pre-open: indexes are sinking the pre-open
September 18, 2020
RegMed Investors’ (RMi) closing bell: follow the bouncing share pricing
September 17, 2020
RegMed Investors’ (RMi) closing bell: the sector got thinned with the prevailing downside trade winds
35 companies, 1 interpreter!
Insight, foresight and recommendation
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