uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 29, 2020
RegMed Investors’ (RMi) pre-open: after a dive, there’s sometimes a jive
June 26, 2020
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector got sacked
June 26, 2020
RegMed Investors’ (RMi) pre-open: stress tests, bad infection news, weakness is driving sentiment’s direction
June 25, 2020
RegMed Investors’ (RMi) closing bell: surge, purge and gorge
June 25, 2020
RegMed Investors’ (RMi) pre-open: negative headlines eat into the upside
June 24, 2020
RegMed Investors’ (RMi) closing bell: infection growth spooks markets as I expected the downslide
June 23, 2020
RegMed Investors’ (RMi) closing bell: sell the green
June 23, 2020
RegMed Investors’ (RMi) pre-open: squeezing the sector’s toothpaste tube…
June 22, 2020
RegMed Investors’ (RMi) closing bell: is the sector a proxy for getting back to some-sort of normal?
June 22, 2020
RegMed Investors’ (RMi) pre-open: is the tank full to travel further RegMed Lane?
35 companies, 1 interpreter!
Insight, foresight and recommendation
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