uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 28, 2020
RegMed Investors’ (RMi) pre-open: trepidation
April 24, 2020
RegMed Investors’ (RMi) closing bell: the upside feels good and shaky in the next weeks
April 24, 2020
RegMed Investors’ (RMi) pre-open: Slippin' and slidin', peepin' and a-hidin', been told along time ago
April 23, 2020
RegMed Investors’ (RMi) closing bell: low volume volatility prevails
April 22, 2020
RegMed Investors’ (RMi) closing bell: the sector is back in an upside groove
April 21, 2020
RegMed Investors’ (RMi) closing bell: they came for the upsiders, put a black bag over their heads and dragged them out
April 21, 2020
RegMed Investors’ (RMi) pre-open: don’t chase Friday’s and Monday’s upside bounces
April 20, 2020
RegMed Investors’ (RMi) closing bell: sector closed positive as indexes dived
35 companies, 1 interpreter!
Insight, foresight and recommendation
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