uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 14, 2016
RegMed’s close: the sector climbs out of its hole
March 11, 2016
RegMed’s close: Sector stocks extend gains …
March 11, 2016
Higher open expected; RegMed sector, beyond financial results, the sector is on pace for what – more volatility?
March 9, 2016
RegMed’s close: momentum is slippin' and-a-slidin' - peepin' and a-hidin'
March 7, 2016
RegMed’s close: the fluctuations in “our” universe come any hour, some days and each week
March 4, 2016
RegMed’s close: up, up and almost away
March 3, 2016
RegMed’s close: the resistance levels are folding
February 26, 2016
RegMed’s close: sector ends higher
February 22, 2016
Higher open expected; RegMed sector still has an appetite for risk
February 19, 2016
RegMed’s close postmortem: good to bad to worse to not so bad again
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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