uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 19, 2023
RegMed Investors (RMi) Closing Bell: sector crumbles after Monday’s stumble
September 18, 2023
RegMed Investors (RMi) Closing Bell: sector stumbles lower
September 15, 2023
RegMed Investors (RMi) Closing Bell: a volatile week ending on a triple-witching Friday
September 14, 2023
RegMed Investors (RMi) Closing Bell: rebound
September 13, 2023
RegMed Investors (RMi) Closing Bell: cell and gene therapy sector runs out of gas
September 12, 2023
RegMed Investors (RMi) Closing Bell: cell and gene therapy sector resembles my slinky
September 11, 2023
RegMed Investors (RMi) Closing Bell: cell and gene therapy sector stays positive
September 8, 2023
RegMed Investors (RMi) Closing Bell: a barely positive sector rebound, better than staring into a share pricing abyss
September 6, 2023
RegMed Investors (RMi) Closing Bell: a lack of sector friction flips with positive force
September 5, 2023
RegMed Investors (RMi) Closing Bell: deep dive to the downside
35 companies, 1 interpreter!
Insight, foresight and recommendation
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