uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 7, 2023
RegMed Investors’ (RMi) closing bell: indexes sell-off after Jerome spoke
March 3, 2023
RegMed Investors’ (RMi) closing bell: sector gets a push pull
March 3, 2023
RegMed Investors’ (RMi) pre-open: a test of strength versus weakness
March 2, 2023
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector’s feeling the lack of sentiment
March 2, 2023
RegMed Investors’ (RMi) pre-open: sector swings back and forth although I basically remain picking short-term indications
March 1, 2023
RegMed Investors’ (RMi) closing bell: the cell/gene therapy sector slumps after mid-day
February 28, 2023
RegMed Investors’ (RMi) closing bell: a volatile February comes to an end as Q4 and FY22 keep rolling out
February 28, 2023
RegMed Investors’ (RMi) pre-open: peaking while seeking acquiescence or validation
February 27, 2023
RegMed Investors’ (RMi) closing bell: hunker down but, be aware of earnings backlash
February 22, 2023
RegMed Investors’ (RMi) closing bell: the sector’s continuous menace - sustainability
35 companies, 1 interpreter!
Insight, foresight and recommendation
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