uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
February 22, 2023
RegMed Investors’ (RMi) pre-open: pick-up a few of the oversold while we wait again for Jerome’s minutes
February 21, 2023
RegMed Investors’ (RMi) closing bell: extending losses as fear defines the cell/gene therapy sector with Q4 and FY22 earnings release bringing more pressures
February 21, 2023
RegMed Investors’ (RMi) pre-open: after a holiday and week of wupp’in
February 15, 2023
RegMed Investors’ (RMi) closing bell: inflation data drags on sector as an end of session closes positive
February 15, 2023
RegMed Investors’ (RMi) pre-open: more sentiment data due
February 14, 2023
RegMed Investors’ (RMi) closing bell: cell/gene therapy sector sell-off deepens as higher inflation reading sent stocks downhill
February 13, 2023
RegMed Investors’ (RMi) closing bell: the sector’s upside bounce was expected
February 10, 2023
RegMed Investors’ (RMi) closing bell: sector shot down by inflationary “objects”
February 7, 2023
RegMed Investors’ (RMi) closing bell: the cell/gene therapy sector suffered tough love until late session to pop the A/D (advance/decline) Line positive
February 1, 2023
RegMed Investors’ (RMi) closing bell: We waited for Jerome – 25-basis points, Godot never really had a day in the limelight
35 companies, 1 interpreter!
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