uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 14, 2023
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March 13, 2023
RegMed Investors’ (RMi) closing bell: sector equities turn up from being oversold clouded by SVB’s decline
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RegMed Investors’ (RMi) closing bell: bad goes to worse and fear for cell and gene therapy sector cash positions
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RegMed Investors’ (RMi) pre-open: probably more down but, almost ready to start buying bottoms
March 9, 2023
RegMed Investors’ (RMi) closing bell: the sector does the limbo dance and low it went?
March 9, 2023
RegMed Investors’ (RMi) pre-open: sector extends the slide while oversold seek value recognition
March 8, 2023
RegMed Investors’ (RMi) closing bell: the cell/gene therapy sector opened down, climbed up and then fell back
March 8, 2023
RegMed Investors’ (RMi) pre-open: just when you thought
35 companies, 1 interpreter!
Insight, foresight and recommendation
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