uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 31, 2023
RegMed Investors’ (RMi) closing bell: a reverse from Monday’s depths
January 31, 2023
RegMed Investors’ (RMi) pre-open: following the Fed as sector share pricing bounces
January 30, 2023
RegMed Investors’ (RMi) closing bell: who said economics don’t matter?
January 27, 2023
RegMed Investors’ (RMi) closing bell: the tide came without a full moon effect
January 27, 2023
RegMed Investors’ (RMi) pre-open: wobble (stagger)or boggle (fear)?
January 26, 2023
RegMed Investors’ (RMi) closing bell: investing in the soft sand at low tide
January 26, 2023
RegMed Investors’ (RMi) pre-open: up, down, round and round goes the sector rope-tide to tan economic data driven market
January 25, 2023
RegMed Investors’ (RMi) closing bell: sector finishes down yet, made strides late in session
January 25, 2023
RegMed Investors’ (RMi) pre-open: share pricing is all over the map as some gains reverse
January 24, 2023
RegMed Investors’ (RMi) closing bell: inclining positive session, yet … wait and watch
35 companies, 1 interpreter!
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