uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 18, 2022
RegMed Investors’ (RMi) closing bell: Why the slide …
April 18, 2022
RegMed Investors’ (RMi) pre-open: the cell and gene therapy sector is ailing
April 14, 2022
RegMed Investors’ (RMi) closing bell: closing with a downslide shortened week with Friday market holiday
April 14, 2022
RegMed Investors’ (RMi) pre-open: curb your enthusiasm
April 12, 2022
RegMed Investors’ (RMi) closing bell: snap, crackle and no pop as liquidity drains from the sector as indexes dives again
April 5, 2022
RegMed Investors’ (RMi) closing bell: rough ride with news spelling share pricing risk
April 4, 2022
RegMed Investors’ (RMi) closing bell: back on top in a tricky environment for cell and gene therapy sector equities
April 1, 2022
RegMed Investors’ (RMi) closing bell: an uptick for the oversold
35 companies, 1 interpreter!
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