uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 1, 2021
RegMed Investors’ (RMi) pre-open: same old volatility tags the sector
September 30, 2021
RegMed Investors’ (RMi) closing bell: sector closes the month with a slip and fall
September 29, 2021
RegMed Investors’ (RMi) closing bell: called it volatile and liquid this a.m., it was
September 27, 2021
RegMed Investors’ (RMi) closing bell: risks are mounting as sentiment seems AWOL
September 23, 2021
Q2/21 Earnings - (LPS - loss-per-share) Results
September 23, 2021
RegMed Investors’ (RMi) closing bell: lucky sector up day with low volume but, risk is still lurking
September 21, 2021
RegMed Investors’ (RMi) closing bell: a buying opportunity for the stem cell and gene therapy sector
September 16, 2021
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector share pricing beat-back quadruple witching
September 14, 2021
RegMed Investors’ (RMi) closing bell: key word for today’s session - fragility
September 10, 2021
RegMed Investors’ (RMi) closing bell: losses accelerated as the session closed
35 companies, 1 interpreter!
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