uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 20, 2019
RegMed Investors’ (RMi) closing bell:the sector closed down after Thursday’s spurt
December 20, 2019
RegMed Investors’ (RMi) pre-open: TGIF
December 19, 2019
RegMed Investors’ (RMi) closing bell: the sector jumped after two down sessions
December 18, 2019
RegMed Investors’ (RMi) closing bell: the sector is counterintuitive as today’s NASDAQ index inclined as my covered composite of companies declined
December 17, 2019
RegMed Investors’ (RMi) closing bell: sector breaks down as profiteering circles the upside
December 16, 2019
RegMed Investors’ (RMi) closing bell: the oversold’s ground moved upward
December 15, 2019
RegMed Investors’ (RMi) closing bell: buying the rumors, selling speculation as the sector gets slammed
December 11, 2019
RegMed Investors’ (RMi) closing bell: review the alternating December Advance/Decline lines
December 11, 2019
RegMed Investors’ (RMi) pre-open: mind your Os
December 10, 2019
RegMed Investors’ (RMi) closing bell: acquisition speculation
35 companies, 1 interpreter!
Insight, foresight and recommendation
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