uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 25, 2021
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October 22, 2021
RegMed Investors’ (RMi) closing bell: a rout that’s been coming
October 21, 2021
RegMed Investors’ (RMi) closing bell: expectation or causation
October 18, 2021
RegMed Investors’ (RMi) closing bell: one word re share pricing - fear
October 15, 2021
RegMed Investors’ (RMi) closing bell: another I foretold you so
October 13, 2021
RegMed Investors’ (RMi) closing bell: a broad-brush approach and sector review
October 11, 2021
RegMed Investors’ (RMi) closing bell: sector’s incline accelerates as session progresses
October 7, 2021
RegMed Investors’ (RMi) closing bell: the oversold were ripe to be picked
October 6, 2021
RegMed Investors’ (RMi) closing bell: stem, cell and gene therapy sector stumbles
October 1, 2021
RegMed Investors’ (RMi) closing bell: Back from the depths to close positive
35 companies, 1 interpreter!
Insight, foresight and recommendation
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