uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 12, 2021
RegMed Investors’ (RMi) closing bell: feeling the squeeze of sentiment
July 9, 2021
RegMed Investors’ (RMi) closing bell: yet another comeback to our upside delight in a changing July
July 8, 2021
RegMed Investors’ (RMi) closing bell: past downslide is an upside for some cell and gene therapy equities
July 7, 2021
RegMed Investors’ (RMi) closing bell: fear while staring down the cell and gene therapy sector abyss
July 3, 2021
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector collapsed after a sloppy week
July 1, 2021
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector bounces after Wednesday’s slight slippage
June 30, 2021
RegMed Investors’ (RMi) closing bell: could have been worse
June 29, 2021
RegMed Investors’ (RMi) closing bell: it was programmed to happen
June 25, 2021
RegMed Investors’ (RMi) closing bell: a good week even with Russell rebalances on a Friday
35 companies, 1 interpreter!
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