uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 3, 2023
RegMed Investors’ (RMi) closing bell: Q2 starts as the cell and gene therapy sector falters
April 3, 2023
RegMed Investors’ (RMi) pre-open: a new month and Q2, do you want the good or bad news?
March 31, 2023
RegMed Investors’ (RMi) closing bell: March and Q1 end on a high note for market and cell and gene therapy sector
March 27, 2023
RegMed Investors’ (RMi) closing bell: a BUY zone or just another algorithm rebound?
March 23, 2023
RegMed Investors’ (RMi) closing bell: momentum interrupts sector’s share pricing bouncing luckily to the upside
March 16, 2023
RegMed Investors’ (RMi) closing bell: sector responds to being oversold reversing some declines
March 16, 2023
RegMed Investors’ (RMi) pre-open: will there be another Black Swan event for the cell and gene therapy sector and how soon versus when?
March 15, 2023
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector suffers from Autophobia
March 15, 2023
RegMed Investors’ (RMi) pre-open: money’s leaving share pricing due to inherent risks
35 companies, 1 interpreter!
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