uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 9, 2023
RegMed Investors’ (RMi) pre-open: will JPM23 stimulate or just ripple share pricing?
January 6, 2023
RegMed Investors’ (RMi) closing bell: jobs economic data pushes market and cell/gene therapy sector uphill
January 3, 2023
RegMed Investors’ (RMi) closing bell: 2023 first session of pain as recessionary perceptions initiated sudden decline
December 30, 2022
RegMed Investors’ (RMi) closing bell: 2022 rushed into its session, week, month and year end with a positive close
December 28, 2022
RegMed Investors’ (RMi) closing bell: sector expectation defined
December 27, 2022
RegMed Investors’ (RMi) closing bell: downside spirals as 2022 fades
December 22, 2022
RegMed Investors’ (RMi) closing bell: selling returned Thursday
December 21, 2022
RegMed Investors’ (RMi) closing bell: two-day confidence bounce
December 20, 2022
RegMed Investors’ (RMi) closing bell: thinking about getting back invested to the sector – DON’T and WAIT
December 19, 2022
RegMed Investors’ (RMi) closing bell: residual negativity haunts our universe of cell and gene therapy is severely damaged
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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