uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 16, 2022
RegMed Investors’ (RMi) pre-open finally Friday
December 15, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector bottoms
December 15, 2022
RegMed Investors’ (RMi) pre-open: the cell and gene therapy sector suffered from indigestion post Jerome’s rate gospel
December 14, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector craters as Fed rate decision unfolds with more hikes next year
December 14, 2022
RegMed Investors’ (RMi) pre-open: waiting for Jerome’s latest interest rate hike decision
December 13, 2022
RegMed Investors’ (RMi) closing bell: indexes slow and some sector gains evaporate post CPI release
December 12, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector opened and closed higher as oversold were “recognized” in-front of CPI and Fed meeting report
December 9, 2022
RegMed Investors’ (RMi) closing bell: the bleed keeps spraying
December 8, 2022
RegMed Investors’ (RMi) closing bell: sector share pricing rise, not due to investors but, electronic trading and algorithms
35 companies, 1 interpreter!
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