uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 7, 2022
RegMed Investors’ (RMi) closing bell: negative reaction
October 7, 2022
RegMed Investors’ (RMi) pre-open: resistance and key jobs report posts the number, 263,000 with unemployment 3.5%
October 6, 2022
RegMed Investors’ (RMi) closing bell: no, good and bad news makes little difference in sector pricing
October 6, 2022
RegMed Investors’ (RMi) pre-open: tick, tock; where’s the price of cell and gene therapy stocks going
October 4, 2022
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector ballooned-up
October 4, 2022
RegMed Investors’ (RMi) pre-open: buy a few dips and a mixed bag of indications
October 3, 2022
RegMed Investors’ (RMi) closing bell: snap, crackle and a pop
September 30, 2022
RegMed Investors’ (RMi) closing bell: closing out September and Q3 with an algorithmic upside “rule”
September 29, 2022
RegMed Investors’ (RMi) closing bell: another I told you so!
September 29, 2022
RegMed Investors’ (RMi) pre-open: what now, after I wrote “sell into any strength”?
35 companies, 1 interpreter!
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