uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 27, 2022
RegMed Investors’ (RMi) closing bell: don’t get use to today’s upside, I believe it’s “transitory”
September 27, 2022
RegMed Investors’ (RMi) pre-open: when you have to take a stock’s value beat-down, just think recovery
September 26, 2022
RegMed Investors’ (RMi) closing bell: playing the bounce game after a very brief upside open
September 26, 2022
RegMed Investors’ (RMi) pre-open: what goes down for five (5) sector moves last week, needs some back-fill
September 21, 2022
RegMed Investors’ (RMi) closing bell: as expected, 0.75 percentage or basis points, let’s be done with the discourse; inflation is NOT going away!
September 19, 2022
News RegMed Investors’ (RMi) pre-open: Investors are getting spooked, reality is a _itch
September 15, 2022
RegMed Investors’ (RMi) closing bell: musical chairs until the melody stops
September 15, 2022
RegMed Investors’ (RMi) pre-open: will sector’s share pricing be risk/reward exposed?
September 14, 2022
RegMed Investors’ (RMi) closing bell: catches a full breath after a deep dive in choppy waters
35 companies, 1 interpreter!
Insight, foresight and recommendation
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