uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 15, 2021
RegMed Investors’ (RMi) pre-open: when you’re on a roller coaster, the only thing you can be sure of is you’ll end up back where you started
January 14, 2021
RegMed Investors’ (RMi) closing bell: the sector gains as markets finish lower
January 13, 2021
RegMed Investors’ (RMi) closing bell: political processes and fiscal aid timing deflates expectation
January 12, 2021
RegMed Investors’ (RMi) closing bell: in which wave are we investing?
January 11, 2021
RegMed Investors’ (RMi) closing bell: Washington tension drains sentiment
January 8, 2021
RegMed Investors’ (RMi) closing bell: the finger came out of the dike of record highs
January 7, 2021
RegMed Investors’ (RMi) closing bell: sector pops in the bubble
January 7, 2021
RegMed Investors’ (RMi) pre-open: markets and sectors remain above the fray
January 6, 2021
RegMed Investors’ (RMi) closing bell: sector sustained as share pricing defies gravity
January 5, 2021
RegMed Investors’ (RMi) closing bell: sector stays up as momentum re-performs
35 companies, 1 interpreter!
Insight, foresight and recommendation
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