uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 6, 2022
RegMed Investors’ (RMi) closing bell: sentiment remains in the toilet, eroding daily and dependent on electronic trading crushing individual investors
December 2, 2022
RegMed Investors’ (RMi) closing bell: The sector is what it is until it isn’t and even then, it doesn’t seem to be
December 2, 2022
RegMed Investors’ (RMi) closing bell: The sector is what it is, until it isn’t and even then, it doesn’t seem to be
November 29, 2022
RegMed Investors’ (RMi) closing bell: the pendulum swung
November 28, 2022
RegMed Investors’ (RMi) closing bell: Being greedy when others are fearful is easier said than done
November 28, 2022
RegMed Investors’ (RMi) pre-open: Ending November this week (Wednesday)
November 25, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector equities faltered Friday in a subdued trading session.
November 25, 2022
RegMed Investors’ (RMi) pre-open: shortened trading session ends week
November 23, 2022
RegMed Investors’ (RMi) closing bell: gobble, gobble; share pricing heated-up
November 22, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy companies are swing to the upside after four (4) declining sessions
35 companies, 1 interpreter!
Insight, foresight and recommendation
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