uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 10, 2022
RegMed Investors’ (RMi) closing bell: share price shredding and destruction continues
June 8, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector rockets altitude
June 7, 2022
RegMed Investors’ (RMi) closing bell: I thought up/downs was an exercise
June 6, 2022
RegMed Investors’ (RMi) pre-open: the tug-of-war in share pricing
June 3, 2022
RegMed Investors’ (RMi) closing bell: when you wish upon a share price
June 3, 2022
RegMed Investors’ (RMi) pre-open: what’s actionable?
May 31, 2022
RegMed Investors’ (RMi) closing bell: difficult to navigate as volatility dives the sector at the month of May ends
May 23, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector declines as market indexes incline
May 19, 2022
RegMed Investors’ (RMi) closing bell: sector was kicked, but not put on its butt
35 companies, 1 interpreter!
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