uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 30, 2022
RegMed Investors’ (RMi) closing bell: tumbling share pricings as inflation and economic data takes its toll
June 29, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector trended upward with the pathway was percentage mixed
June 28, 2022
RegMed Investors’ (RMi) pre-open: snap, crackle and pop
June 27, 2022
RegMed Investors’ (RMi) closing bell: oversold as volatility ain’t over
June 24, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector gets a spanking
June 23, 2022
RegMed Investors’ (RMi) closing bell: which way forward? SELL into Strength, come back post earnings
June 21, 2022
RegMed Investors’ (RMi) closing bell: sector boomed today, what’s sustainable and for how long?
June 16, 2022
RegMed Investors’ (RMi) closing bell: the rise and fall of the cell and gene therapy space
June 13, 2022
RegMed Investors’ (RMi) closing bell: shaken, rattled and then rolled with no place to hide
June 13, 2022
RegMed Investors’ (RMi) pre-open: climbing the rope of share pricing and failing again
35 companies, 1 interpreter!
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